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Human gene therapy clinical development

Human gene therapy clinical development
紙雑誌
Mary Ann Liebert<Z78-A838>
国立国会図書館全国の図書館
  • ISSN2324-8637
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MiR-625-5p Inhibits Cardiac Hypertrophy Through Targeting STAT3 and CaMKII

MiR-625-5p Inhibits Cardiac Hypertrophy Through Targeting STAT3 and CaMKII
デジタル記事
2019-12-01Human Gene Therapy Clinical Development30 4p.182-191
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Inhibition of miR-203 Ameliorates Osteoarthritis Cartilage Degradation in the Postmenopausal Rat Model: Involvement of Estrogen Receptor α

Inhibition of miR-203 Ameliorates Osteoarthritis Cartilage Degradation in the Postmenopausal Rat Model: Involvement of Estrogen Receptor α
デジタル記事
2019-12-01Human Gene Therapy Clinical Development30 4p.160-168
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The Genetically Modified Organism Medicinal Framework in Europe, United States, and Japan: Underlying Scientific Principles and Considerations Toward the Development of Gene Therapy and Genetically Modified Cell-Based Products

The Genetically Modified Organism Medicinal Framework in Europe, United States, and Japan: Underlying Scientific Principles and Considerations Toward the Development of Gene Therapy and Genetically Modified Cell-Based Products
デジタル記事
2019-09-01Human Gene Therapy Clinical Development30 3p.114-128
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A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease

A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease
デジタル記事
2019-03Human Gene Therapy Clinical Development30 1p.29-39
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Long-Term Follow-Up of a Phase I/II Study of ProSavin, a Lentiviral Vector Gene Therapy for Parkinson's Disease

Long-Term Follow-Up of a Phase I/II Study of ProSavin, a Lentiviral Vector Gene Therapy for Parkinson's Disease
デジタル記事
2018-09Human Gene Therapy Clinical Development29 3p.148-155
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Gene Therapy for Osteoarthritis: Pharmacokinetics of Intra-Articular Self-Complementary Adeno-Associated Virus Interleukin-1 Receptor Antagonist Delivery in an Equine Model

Gene Therapy for Osteoarthritis: Pharmacokinetics of Intra-Articular Self-Complementary Adeno-Associated Virus Interleukin-1 Receptor Antagonist Delivery in an Equine Model
デジタル記事
2018-06Human Gene Therapy Clinical Development29 2p.90-100
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AAVrh.10-Mediated APOE2 Central Nervous System Gene Therapy for APOE4-Associated Alzheimer's Disease

AAVrh.10-Mediated APOE2 Central Nervous System Gene Therapy for APOE4-Associated Alzheimer's Disease
デジタル記事
2018-03Human Gene Therapy Clinical Development29 1p.24-47
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Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-<i>hGAA</i>) Gene Therapy in Children Affected by Pompe Disease

Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-<i>hGAA</i>) Gene Therapy in Children Affected by Pompe Disease
デジタル記事
2017-12Human Gene Therapy Clinical Development28 4p.208-218
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Persistent Expression of Dopamine-Synthesizing Enzymes 15 Years After Gene Transfer in a Primate Model of Parkinson's Disease

Persistent Expression of Dopamine-Synthesizing Enzymes 15 Years After Gene Transfer in a Primate Model of Parkinson's Disease
デジタル記事
2017-06Human Gene Therapy Clinical Development28 2p.74-79
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Establishing a Large-Animal Model for <i>In Vivo</i> Reprogramming of Bile Duct Cells into Insulin-Secreting Cells to Treat Diabetes

Establishing a Large-Animal Model for <i>In Vivo</i> Reprogramming of Bile Duct Cells into Insulin-Secreting Cells to Treat Diabetes
デジタル記事
2017-06Human Gene Therapy Clinical Development28 2p.87-95
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Non-Clinical Study Examining AAV8.TBG.hLDLR Vector-Associated Toxicity in Chow-Fed Wild-Type and LDLR<sup>+/−</sup>Rhesus Macaques

Non-Clinical Study Examining AAV8.TBG.hLDLR Vector-Associated Toxicity in Chow-Fed Wild-Type and LDLR<sup>+/−</sup>Rhesus Macaques
デジタル記事
2017-03Human Gene Therapy Clinical Development28 1p.39-50
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Nonclinical Pharmacology/Toxicology Study of AAV8.TBG.mLDLR and AAV8.TBG.hLDLR in a Mouse Model of Homozygous Familial Hypercholesterolemia

Nonclinical Pharmacology/Toxicology Study of AAV8.TBG.mLDLR and AAV8.TBG.hLDLR in a Mouse Model of Homozygous Familial Hypercholesterolemia
デジタル記事
2017-03Human Gene Therapy Clinical Development28 1p.28-38
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Rationale and Design of a Phase 1 Clinical Trial to Evaluate HSV G207 Alone or with a Single Radiation Dose in Children with Progressive or Recurrent Malignant Supratentorial Brain Tumors

Rationale and Design of a Phase 1 Clinical Trial to Evaluate HSV G207 Alone or with a Single Radiation Dose in Children with Progressive or Recurrent Malignant Supratentorial Brain Tumors
デジタル記事
2017-03Human Gene Therapy Clinical Development28 1p.7-16
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Optimizing Transgene Configuration and Protein Fusions to Maximize Dopamine Production for the Gene Therapy of Parkinson's Disease

Optimizing Transgene Configuration and Protein Fusions to Maximize Dopamine Production for the Gene Therapy of Parkinson's Disease
デジタル記事
2016-09Human Gene Therapy Clinical Development27 3p.100-110
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Safety Studies in Tumor and Non-Tumor-Bearing Mice in Support of Clinical Trials Using Oncolytic VSV-IFNβ-NIS

Safety Studies in Tumor and Non-Tumor-Bearing Mice in Support of Clinical Trials Using Oncolytic VSV-IFNβ-NIS
デジタル記事
2016-09Human Gene Therapy Clinical Development27 3p.111-122
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Investor Outlook: Rising from the Ashes; GSK's European Approval of Strimvelis for ADA-SCID

Investor Outlook: Rising from the Ashes; GSK's European Approval of Strimvelis for ADA-SCID
デジタル記事
2016-06Human Gene Therapy Clinical Development27 2p.57-61
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Design of a Phase I Clinical Trial to Evaluate M032, a Genetically Engineered HSV-1 Expressing IL-12, in Patients with Recurrent/Progressive Glioblastoma Multiforme, Anaplastic Astrocytoma, or Gliosarcoma

Design of a Phase I Clinical Trial to Evaluate M032, a Genetically Engineered HSV-1 Expressing IL-12, in Patients with Recurrent/Progressive Glioblastoma Multiforme, Anaplastic Astrocytoma, or Gliosarcoma
デジタル記事
2016-06Human Gene Therapy Clinical Development27 2p.69-78
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Use of Adeno-Associated Virus to Enrich Cardiomyocytes Derived from Human Stem Cells

Use of Adeno-Associated Virus to Enrich Cardiomyocytes Derived from Human Stem Cells
デジタル記事
2015-09Human Gene Therapy Clinical Development26 3p.194-201
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Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning

Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning
デジタル記事
2015-09Human Gene Therapy Clinical Development26 3p.185-193
全国の図書館