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Human Gene Therapy

Human Gene Therapy
紙雑誌
Mary Ann Liebert<Z54-J358>
国立国会図書館全国の図書館
  • ISSN1043-0342
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Hematopoietic stem cell gene therapy corrects neuropathic phenotype in murine model of mucopolysaccharidosis type II.

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Hematopoietic stem cell gene therapy corrects neuropathic phenotype in murine model of mucopolysaccharidosis type II.
デジタル博士論文障害者向け資料あり
若林, 太一, ワカバヤシ, タイチ, Wakabayashi, Taichi2017-04-11Human gene therapy
国立国会図書館
  • ISSN1043-0342

Concise Analysis of Single-Stranded DNA of Recombinant Adeno-Associated Virus By Automated Electrophoresis System

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デジタル記事
苑, 宇哲, Higashiyama, Kiyoko, Hashiba, Noriko, 増見, 恭子, 遊佐, 敬介, 内田, 和久Mary Ann Liebert2024-02-15Human Gene Therapy35 3-4p.104-113
インターネットで読める全国の図書館
  • 掲載誌（ISSN）1043-0342 1557-7422

Concise Analysis of Single-Stranded DNA of Recombinant Adeno-Associated Virus By Automated Electrophoresis System

Concise Analysis of Single-Stranded DNA of Recombinant Adeno-Associated Virus By Automated Electrophoresis System
デジタル記事
2024-02-15Human Gene Therapy35 3-4p.104-113
インターネットで読める全国の図書館

Quantitation of Residual Host Cell DNA in Recombinant Adeno-Associated Virus Using Droplet Digital Polymerase Chain Reaction

Quantitation of Residual Host Cell DNA in Recombinant Adeno-Associated Virus Using Droplet Digital Polymerase Chain Reaction
デジタル記事
2023-06Human Gene Therapy34 11-12p.578-585
インターネットで読める全国の図書館

Quantitation of Residual Host Cell DNA in Recombinant Adeno-Associated Virus Using Droplet Digital Polymerase Chain Reaction

Quantitation of Residual Host Cell DNA in Recombinant Adeno-Associated Virus Using Droplet Digital Polymerase Chain Reaction
デジタル記事
Higashiyama, Kiyoko, 苑, 宇哲, Hashiba, Noriko, 増見, 恭子, 遊佐, 敬介, 内田, 和久Mary Ann Liebert2023-06Human Gene Therapy34 11-12p.578-585
インターネットで読める全国の図書館
  • 掲載誌（ISSN）1043-0342 1557-7422

Novartis Confirms Deaths of Two Patients Treated with Gene Therapy Zolgensma

Novartis Confirms Deaths of Two Patients Treated with Gene Therapy Zolgensma
デジタル記事
2022-09-01Human Gene Therapy33 17-18p.842-844
全国の図書館

Insight and Development of Advanced Recombinant Adeno-Associated Virus Analysis Tools Exploiting Single-Particle Quantification by Multidimensional Droplet Digital PCR

Insight and Development of Advanced Recombinant Adeno-Associated Virus Analysis Tools Exploiting Single-Particle Quantification by Multidimensional Droplet Digital PCR
デジタル記事
2022-09-01Human Gene Therapy33 17-18p.977-989
全国の図書館

Enhanced Delivery of Ligand-Conjugated Antisense Oligonucleotides (C16-HA-ASO) Targeting Dystrophia Myotonica Protein Kinase Transcripts for the Treatment of Myotonic Dystrophy Type 1

Enhanced Delivery of Ligand-Conjugated Antisense Oligonucleotides (C16-HA-ASO) Targeting Dystrophia Myotonica Protein Kinase Transcripts for the Treatment of Myotonic Dystrophy Type 1
デジタル記事
2022-08-01Human Gene Therapy33 15-16p.810-820
全国の図書館

Adeno-Associated Virus-Mediated Gene Therapy for Patients' Fibroblasts, Induced Pluripotent Stem Cells, and a Mouse Model of Congenital Adrenal Hyperplasia

Adeno-Associated Virus-Mediated Gene Therapy for Patients' Fibroblasts, Induced Pluripotent Stem Cells, and a Mouse Model of Congenital Adrenal Hyperplasia
デジタル記事
2022-08-01Human Gene Therapy33 15-16p.801-809
全国の図書館

Food and Drug Administration Lifts Clinical Hold on Pfizer Duchenne Muscular Dystrophy Gene Therapy Linked to Patient Death

Food and Drug Administration Lifts Clinical Hold on Pfizer Duchenne Muscular Dystrophy Gene Therapy Linked to Patient Death
デジタル記事
2022-06-01Human Gene Therapy33 11-12p.573-576
全国の図書館

Efficacy and Safety of a Krabbe Disease Gene Therapy

Efficacy and Safety of a Krabbe Disease Gene Therapy
デジタル記事
2022-05-01Human Gene Therapy33 9-10p.499-517
全国の図書館

Higher Seroprevalence of Anti-Adeno-Associated Viral Vector Neutralizing Antibodies Among Racial Minorities in the United States

Higher Seroprevalence of Anti-Adeno-Associated Viral Vector Neutralizing Antibodies Among Racial Minorities in the United States
デジタル記事
2022-04-01Human Gene Therapy33 7-8p.442-450
全国の図書館

Nonhuman Primate Adenoviruses of the Human Adenovirus B Species Are Potent and Broadly Acting Oncolytic Vector Candidates

Nonhuman Primate Adenoviruses of the Human Adenovirus B Species Are Potent and Broadly Acting Oncolytic Vector Candidates
デジタル記事
2022-03-01Human Gene Therapy33 5-6p.275-289
全国の図書館

Size Exclusion Chromatography with Dual Wavelength Detection as a Sensitive and Accurate Method for Determining the Empty and Full Capsids of Recombinant Adeno-Associated Viral Vectors

Size Exclusion Chromatography with Dual Wavelength Detection as a Sensitive and Accurate Method for Determining the Empty and Full Capsids of Recombinant Adeno-Associated Viral Vectors
デジタル記事
2022-02-01Human Gene Therapy33 3-4p.202-212
全国の図書館

Higher Transduction Efficiency of AAV5 to Neural Stem Cells and Immature Neurons in Gerbil Dentate Gyrus Compared to AAV2 and rh10

Higher Transduction Efficiency of AAV5 to Neural Stem Cells and Immature Neurons in Gerbil Dentate Gyrus Compared to AAV2 and rh10
デジタル記事
2022-01-01Human Gene Therapy33 1-2p.76-85
全国の図書館

Neutralizing Antibody Evasion and Transduction with Purified Extracellular Vesicle-Enveloped Adeno-Associated Virus Vectors

Neutralizing Antibody Evasion and Transduction with Purified Extracellular Vesicle-Enveloped Adeno-Associated Virus Vectors
デジタル記事
2021-12-01Human Gene Therapy32 23-24p.1457-1470
全国の図書館

Long-Term Follow-Up of Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy

Long-Term Follow-Up of Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy
デジタル記事
2021-10-01Human Gene Therapy32 19-20p.1260-1269
全国の図書館

Capsid-Engineering for Central Nervous System-Directed Gene Therapy with Adeno-Associated Virus Vectors

Capsid-Engineering for Central Nervous System-Directed Gene Therapy with Adeno-Associated Virus Vectors
デジタル記事
2021-10-01Human Gene Therapy32 19-20p.1096-1119
全国の図書館

Fourth Boy Dies in Clinical Trial of Astellas' AT132

Fourth Boy Dies in Clinical Trial of Astellas' AT132
デジタル記事
2021-10-01Human Gene Therapy32 19-20p.1008-1010
全国の図書館